The Latest Developments on the Gene Therapy Frontier

Gene therapy is once again at the forefront of biomedical research, catalyzed by advances in safer delivery of genes to cells. Science may also move quickly past gene replacement therapy to gene editing via CRISPR and other methods, an approach in which the unknowns are even greater and clinical results are just beginning to emerge.

INCLUDED IN THIS TRENDLINE

  • BioMarin finally secures FDA approval of hemophilia gene therapy
  • Cell and gene therapy manufacturing: the next generation of startups
  • Vertex taking ‘flexible’ approach to payment talks for experimental CRISPR therapy

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